2025 PGROD - Making the Diagnosis When It Counts: Recognizing Treatable Leukodystrophies by Florian Eichler, MD

Please read and follow instructions

Thursday, March 27, 2025, 12:00 AM - Tuesday, March 27, 2029, 11:59 PM


AMA PRA Category 1 Credits™ (1.00 hours), AAPA Credit(s) (1.00 hours), ACPE Contact Hour(s) (1.00 hours), ANCC Contact Hour(s) (1.00 hours), APA Credit(s) (1.00 hours), IPCE Credit(s) (1.00 hours), Non-Physician Attendance (1.00 hours)

Pediatric Grand Rounds provides a forum for recognized experts to present state-of-the-art information regarding diagnosis and treatment of pediatric diseases, outline diagnostic approaches, provide updates on new research, and discuss clinical management related to the care and management of the pediatric patient. Pediatric Grand Rounds is held every Thursday from 8-9am.

Objective(s): 1 Explain how pathophysiology informs trial design for the leukodystrophies. 2 Discuss the different gene therapy approaches for the leukodystrophies. 3 Describe biomarkers monitoring and management of leukodystrophy trials.
Location: Nationwide Children's Hospital Conference Center
Specialties: General Pediatrics

Faculty Disclosures:
Florian Eichler, MD (Consulting Fee-Atlas Venture|Consulting Fee-ASPA Therapeutucs|Consulting Fee-Acadia|Consulting Fee-Leal Therapeutics|Consulting Fee-Orchard Therapeutics|Consulting Fee-Sanofi Therapeutics|Consulting Fee-Spoila Therapeutics|Consulting Fee-Spur Therapeutics|Consulting Fee-Takeda Therapeutics|Consulting Fee-Up to Date|Grant or research support-GLIA CTN|Grant or research support-European Leukodystrophy Associateion|Ownership-Swan Bio - 03/21/2025)
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1. Explain how pathophysiology informs trial design for the leukodystrophies.
2. Discuss the different gene therapy approaches for the leukodystrophies.
3. Describe biomarkers monitoring and management of leukodystrophy trials.

In support of improving patient care, Nationwide Children's Hospital is jointly accredited by the Accreditation Council for Continuing Medical Education (ACCME), the American Nurses Credentialing Center (ANCC),  and the Accreditation Council for Pharmacy Education (ACPE), to provide continuing medical education for the healthcare team.

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Cancellations received in writing no less than 20 days before the course will be refunded, less a 20% administrative fee. No refunds will be made on cancellations received after that date. Please send cancellation requests to [email protected].

Nationwide Children's Hospital reserves the right to cancel or postpone this program if necessary; in the event of cancellation, course fees will be fully refunded. We are not responsible for other costs incurred such as non-refundable airline tickets or hotel penalties.

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Nationwide Children's Hospital adheres to the ACCME’s Standards for Integrity and Independence in Accredited Continuing Education. Any individuals in a position to control the content of a CE activity, including faculty, planners, reviewers or others are required to disclose all relevant financial relationships with ineligible entities (commercial interests). All relevant conflicts of interest have been mitigated prior to the commencement of the activity.